ITF Therapeutics LLC, the U.S. rare disease affiliate of Italfarmaco, today announced that one oral and nine poster presentations have been accepted at the Muscular Dystrophy Association (MDA) ...

Roche’s autoimmune drug Enspryng is making solid progress as a treatment for neuromyelitis optica spectrum disorder (NMOSD).

Interim clinical study results for the BB-301 Phase 1b/2a Treatment Study including 12-month follow-up results for the first four Cohort 1 ...

Illinois nurse Sarah A. Delashmit faked cancer and also 'stole' someone's disease after working at a summer camp for adults ...

Late-breaking poster to feature new positive cardiopulmonary function results from the DELIVER trial of z-rostudirsen in DMD -- Oral ...

Eric Dane, known for his roles on "Grey's Anatomy" and "Euphoria," died this week from amyotrophic lateral sclerosis at age 53.

Eric Dane died on Thursday, Feb. 19, less than a year after he was diagnosed with ALS. The life expectancy for many is three ...

Dyne Therapeutics Inc. (NASDAQ: DYN) is one of the 13 hot stocks to buy with the highest upside potential. As of February 13, ...

Del-desiran (also known as AOC1001) is an antibody-oligonucleotide conjugate comprised of a DMPK small interfering RNA (siRNA ...

A preclinical study led by the Germans Trias i Pujol Research Institute (IGTP), in collaboration with the Institut de ...