Scientists at The University of Texas at Austin have developed a revolutionary gene-editing method using bacterial retrons that can correct multiple disease-causing mutations at once. Unlike ...

For the millions of people who carry the gene APOE4, the strongest known genetic risk factor for Alzheimer's disease, their brain activity may begin changing long before any memory problems appear.

The first-ever clinical trial of an adeno-associated virus (AAV) gene therapy for type 1 diabetes (T1D) is set to begin this year. The PROGRESS study will enroll adults with T1D to receive a one-time ...

In 1976, Richard Dawkins published a book titled after an idea he’d come up with while teaching a lecture on animal behaviour for his PhD supervisor. It just so happened that the idea of The Selfish ...

Andrew Czerwinski is reminded at every practice, at every home game he has with the Somers boys basketball team every time he looks at the gym's wall. There he sees a banner with a list of the ...

The authors describe the scientific foundations of a study of gene therapy for hearing loss caused by damaging variants in the gene OTOF. Department of Otorhinolaryngology and Head and Neck Surgery, ...

UniQure needs to run another study to prove its gene therapy "actually helps people with Huntington's disease," a senior FDA official said. The official said UniQure is the "latest company to make a ...

A pioneering gene therapy could help treat a rare seizure disorder called Dravet syndrome, according to new clinical trial results. The drug, called zorevunersen, holds promise, especially for people ...